Immune systems of ‘bubble babies’ restored by gene therapy
Dr. Donald Kohn, professor of Microbiology, Immunology, & Molecular Genetics, and member of the Eli and Edythe Broad Center of Regenerative Medicine and Stem Cell Research, and his colleagues have demonstrated that a combination of chemotherapy and gene therapy may help doctors treat children with “bubble boy” disease, in which the body cannot successfully fight off germs.